Consideration will be given to
research projects developing new therapies for NPC as well as those designed to complement therapies presently in the pipeline (upon confirming no redundancies exist i.e. multiple dosing studies on pipeline drugs.) Consideration will further be given to gene therapy proposals.
Research exploring psychiatric issues impacting quality of life through the lifespan of the patient population and research projects that improve our understanding of the biology, pathogenesis and disease state and have a direct impact on translation of new treatments to patients is encouraged. Studies looking to understand variants in the population to formulate targeted supportive care and therapy are welcome.