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To promote the development and testing of therapeutics to treat and reverse Rett syndrome (RTT). Awards will be provided for cell-based assay development, early-stage drug discovery and development, early stage medicinal chemistry efforts on high value candidate therapeutics, cell-based screening of candidate therapeutics and follow-on early-stage in vivo testing. Grant applications for exploratory studies towards development of biomarkers or objective clinical outcome measures will also be considered. The goal of this award mechanism is to provide seed funding for early stage drug discovery and development efforts.